Neurology

Huntington's disease: genetic and progressive

A rare hereditary neurodegenerative disease

Dr. Antoine Mercier

Neurologist

6 min read
Huntington's disease: genetic and progressive

An autosomal dominant disease

Huntington's is due to abnormal CAG repeat expansion in the HTT gene. Onset typically 30-50 years. Each child of an affected person has a 50% risk.

Symptoms

Motor (chorea: involuntary jerky movements), cognitive (executive functions, memory), psychiatric (depression, irritability, apathy). Progression over 15-20 years.

Diagnosis

Genetic test (CAG repeat count). Predictive testing with mandatory genetic counseling and psychological follow-up.

Treatments

  • Tetrabenazine, deutetrabenazine: chorea
  • Antidepressants, antipsychotics for psychiatric symptoms
  • Speech and physical therapy
  • Antisense oligonucleotides under research (tominersen)

Care

Multidisciplinary specialized centers, patient associations, advance care planning.

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